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13 Mar, 2025

Racing Against Time: the Torbert Family’s Story

"MPS II, also known as Hunter Syndrome, has been a part of my life for as long as I can remember. I grew...

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7 Nov, 2024

Researcher and Advocate: Dr. Kakkis

In the early days of his career, a young scientist named Emil Kakkis found himself deep in the world of...

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5 Sep, 2024

Update on RGX-121 Treatment for MPS II

The National MPS Society is pleased to share an update on RGX-121, an investigational gene therapy for MPS II...

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4 Sep, 2024

Denali Therapeutics Announces Plans to File for Accelerated Approval of Tividenofusp Alfa (DNL310) for the Treatment of MPS II

After recent successful meetings with the FDA, Denali Therapeutics announced its plan to file for accelerated...

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22 Sep, 2022

Newborn Screening Article Release

Matthew Ellinwood, Chief Scientific Officer, authored a new publication published in the American Journal of...

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3 Aug, 2022

DHHS adds MPS II to the RUSP for Newborn Screening in the United States

Click here to download full text.Durham, NC August 3, 2022 - The National MPS Society announces that...

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