Small But Mighty: Kashton (MPS II) On any given afternoon in Oklahoma, you can expect to find two-year-old...
September is National Newborn Screening Awareness Month—a time to reflect on the life-saving power of early...
"MPS II, also known as Hunter Syndrome, has been a part of my life for as long as I can remember. I grew...
In the early days of his career, a young scientist named Emil Kakkis found himself deep in the world of...
The National MPS Society is pleased to share an update on RGX-121, an investigational gene therapy for MPS II...
After recent successful meetings with the FDA, Denali Therapeutics announced its plan to file for accelerated...
