The Annual Fund helps the Society provide funding for several key programs like Family Support, Pathways, and more.
Join us in Orlando, FL, from December 19th to the 21st. You can click the register now button to visit our conference registration site and learn more. We look forward to celebrating the 50th anniversary of the National MPS Society with MPS/ML friends and family from across the nation!
Our mission is to serve those impacted by mucopolysaccharidosis (MPS) and mucolipidosis (ML). These are rare genetic diseases with no cures. We support research, provide families with invaluable resources, and work to increase public and professional awareness.
Have you or your child recently been diagnosed with MPS or ML, or is your child undergoing diagnostic testing? We are here to help and can connect you with the information you need.
Donations to the National MPS Society allow us to support families affected by MPS and ML, fund medical research to find cures for these diseases and keep the public engaged and informed.
Families are the linchpin of our community, and whether it’s financial assistance during a hard time, a special treat for an affected family member or to help make educational dreams come true, we support MPS and ML families across the nation.
We raise money to provide student fellowships and fund research projects. We participate in and host technical conferences that allow researchers to collaborate. We collaborate with other patient support groups and foundations to fund research. Learn about our recent grants and research updates.
Let us introduce you to Jacob Ray (J.R.) Anton, one of the many faces of MPS. J.R., who passed away in May…
The National MPS Society is pleased to share an update on RGX-121, an investigational gene therapy for MPS II (also…
After recent successful meetings with the FDA, Denali Therapeutics announced its plan to file for accelerated…
Please help us find a cure and help those in need.
Links for Lucas Golf Outing Hosted by Lew and Stacey Montgomery
Join us for the 5th Annual John “Lepe” Loy Memorial Golf Tournament Hosted by Don and Lynda Witte
Join us virtually for the 15th Annual cabi Fashion Fundraiser Hosted by Lynn Hopkins
We are so pleased to share this update on RGX-121, an investigational gene therapy for #MPSII (#HunterSyndrome), from REGENXBIO! Updates like these always lift our spirits, as continued research and new treatments mean we are growing ever closer to finding a cure for all types of #MPS.
If you'd like to read more about this therapy and its trial results, please visit their website: ow.ly/eUo350Tgvek
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REMINDER: the Adult Resource Committee is hosting a social hour this Friday, September 6, at 8 PM EST! Register now: ow.ly/1CVF50SZwzp
#MPS #ml #raredisease #hurlersyndrome #HunterSyndrome #sanfilippo #morquiosyndrome #maroteauxlamysyndrome #slysyndrome #hyaluronidasesyndromeAffected individuals aged 16 or older are invited to join the Adult Resources Committee on Friday, September 6, at 8 P.M. EST for a social event via Zoom! Register now and be sure to join the call, where you'll have an opportunity to connect and socialize with other people who have MPS & ML: ow.ly/1CVF50SZwzp
#MPS #ML #RareDisease #HurlerSyndrome #HunterSyndrome #Sanfilippo #MorquioSyndrome #MaroteauxLamySyndrome #SlySyndrome #HyaluronidaseSyndrome
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In case you missed it: Society members Christopher & Jacob Hohn recently won one of Sanofi's coveted 2024 TORCH Awards! Congratulations to two very deserving winners 💜
Watch the video now: ow.ly/hWsB50T8Zn7
#MPS #ML #MPSI #RareDisease #HurlerSyndrome
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Love to the family Hohn from another MPS1 family in Sweden 🇸🇪💜❤️
Congrats to Christopher & Jacob! 💜💜
