We hope you are planning on joining us in Orlando, FL, from December 19-21, 2024, for our 38th Annual...
In the early days of his career, a young scientist named Emil Kakkis found himself deep in the world of...
We hope you are planning on joining us in Orlando, FL, from December 19-21, 2024, for our 38th Annual...
Our 2024 Fall edition of Courage is now available electronically to view or download! Click to read the...
"I was born with a rare disease without even knowing it," explains Fanny Z., a 14-year member of the Society...
Lucas was the youngest of four children. From the start, he stood out—not just as the baby of the family, but...
From Terri Klein, President & CEO: Over four years ago, Dr. Matthew Ellinwood came to work...
Benji C. is a strong, confident, self-assured, loud, and determined 8-year-old with MPS I. When Benji was...
