Each year we remember individuals with MPS and ML who have passed away but who remain in our thoughts and hearts. We invite you to join us in reading about and remembering our cherished friends and family.
New Frequently Asked Questions on COVID-19, vaccine distribution, and the impacts on the rare disease community. Click through for some common answers from our CSO and Scientific Advisory Board.
Our December issue of printed Courage is out now, just in time for the holidays! It features 60 full-color pages of stories, family spotlights, program updates, science & research news, fundraising efforts, and more.
Join in on this celebrated day to give. Help us reach our $50,000 goal by making a donation today!
Re-watch the informative conversation with Elsa Shapiro, PhD and Paul Harmatz, MD, on the unique role of the consulting psychologist, building partnerships within the greater trial ecosystem, and considerations for protocol development.
The annual award recognizes exceptional patient leadership advocacy in the field of lysosomal disease. Presentation will take place Monday, February 8, 2021 at the 17th Annual WORLDSymposium.
The recommended framework would qualify many individuals with MPS and ML to be among the first recipients of a COVID-19 vaccine when it becomes available.
National MPS Society Bake Sale and Bake Off starts October 30 - November 7!
Our Virtual Family Conference has concluded but registered attendees can still access it on-demand through October 12th!
Now recruiting patients born in: California, Michigan, New Jersey, New York This study is also recruiting any patients in any state who have privately banked cord blood and would provide a single-drop sample. Please contact Leslie Urdaneta directly if interested. This study is recruiting patients with MPS I (attenuated: Hurler-Scheie or Scheie Syndromes), MPS II, … Continued