Clinical Trials

Clinical Trial for MPS DiseasesClinical trials are research studies that determine whether treatments or devices are safe for humans. These studies also look for effective medical approaches for MPS and ML and help provide reliable data for patients, researchers and doctors. Clinical trials are conducted on small groups to determine whether a drug or procedure causes negative reactions or unsatisfactory side effects.

As clinical trial updates happen frequently, please check clinicaltrials.gov for up to date information on clinical trials, observational and natural history studies.

Questions about clinical trials?

Read personal stories of people who participated in clinical trials.

Glossary of clinical research terms.

Our Mission

The National MPS Society exists to cure, support and advocate for MPS and ML.

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