Lucas was the youngest of four children. From the start, he stood out—not just as the baby of the family, but...
From Terri Klein, President & CEO: Over four years ago, Dr. Matthew Ellinwood came to work...
Benji C. is a strong, confident, self-assured, loud, and determined 8-year-old with MPS I. When Benji was...
The National MPS Society is pleased to share an update on RGX-121, an investigational gene therapy for MPS II...
After recent successful meetings with the FDA, Denali Therapeutics announced its plan to file for accelerated...
An Update on Allievex Dearest Sanfilippo Community Members and Allies, It is with deep...
Angels Among Us: Remembering Our Loved Ones Each year, we remember individuals with MPS or...
You are invited to join us in Bethesda, Maryland for our 37th Annual Family Conference! Located just outside...
