An Update on Allievex Dearest Sanfilippo Community Members and Allies, It is with deep...
Click here to download full text.Durham, NC August 3, 2022 - The National MPS Society announces that...
The Assistance Fund, an independent charitable patient assistance foundation that helps patients and families...
The U.S. Food and Drug Administration today approved Mepsevii (vestronidase alfa-vjbk) to treat pediatric and...
Sangamo Therapeutics treated its first patient in the Phase 1/2 clinical trial ("the CHAMPIONS study")...
