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Press Releases

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  • Topic: Research
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15 Apr, 2025

National MPS Society Applauds Renewed Progress for TA-ERT (MPS IIIB) Program Under Spruce Biosciences Leadership

Durham, NC — April 15, 2025 — The National MPS Society welcomes the news that Spruce Biosciences is now...

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31 Mar, 2025

National MPS Society Responds to Dr. Peter Marks’ Resignation

The Society praises Dr. Marks' leadership at the FDA and urges continued strong leadership to advance MPS...

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7 Nov, 2024

Researcher and Advocate: Dr. Kakkis

In the early days of his career, a young scientist named Emil Kakkis found himself deep in the world of...

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24 Jul, 2024

Update on Allievex and AX 250

 An Update on Allievex  Dearest Sanfilippo Community Members and Allies, It is with deep...

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3 Aug, 2022

DHHS adds MPS II to the RUSP for Newborn Screening in the United States

Click here to download full text.Durham, NC August 3, 2022 - The National MPS Society announces that...

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30 Nov, 2017

Financial help available for MPS VII patients

The Assistance Fund, an independent charitable patient assistance foundation that helps patients and families...

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15 Nov, 2017

FDA approves MPS VII drug

The U.S. Food and Drug Administration today approved Mepsevii (vestronidase alfa-vjbk) to treat pediatric and...

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14 Nov, 2017

Sangamo treats first patient with gene therapy

Sangamo Therapeutics treated its first patient in the Phase 1/2 clinical trial ("the CHAMPIONS study")...

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