Join us at Dorothea Dix Park on March 26, 2022 for the Raleigh Run for Rare. For more information, click...
Accelerating a Treatment for GNTAB-Related Disorders Richard Steet, Ph.D.Jennifer Klein, MS One...
For years, families have recognized sleeping disorders are manifestations of Mucolipidosis (ML) II, II/III...
T. Klein, President and CEONational MPS SocietyJ. Noble, Vice Chair ISMRD Children with Mucolipidosis...
Although originally thought to be two separate diseases, ML II and ML III are both caused by deficiencies of...