The National MPS Society is pleased to share an update on RGX-121, an investigational gene therapy for MPS II...
After recent successful meetings with the FDA, Denali Therapeutics announced its plan to file for accelerated...
Matthew Ellinwood, Chief Scientific Officer, authored a new publication published in the American Journal of...
Click here to download full text.Durham, NC August 3, 2022 - The National MPS Society announces that...
Download Full Text Durham, NC February 11, 2022 - The National MPS Society announces that the Advisory...
Sangamo Therapeutics treated its first patient in the Phase 1/2 clinical trial ("the CHAMPIONS study")...
