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5 Sep, 2024

Update on RGX-121 Treatment for MPS II

The National MPS Society is pleased to share an update on RGX-121, an investigational gene therapy for MPS II...

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4 Sep, 2024

Denali Therapeutics Announces Plans to File for Accelerated Approval of Tividenofusp Alfa (DNL310) for the Treatment of MPS II

After recent successful meetings with the FDA, Denali Therapeutics announced its plan to file for accelerated...

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22 Sep, 2022

Newborn Screening Article Release

Matthew Ellinwood, Chief Scientific Officer, authored a new publication published in the American Journal of...

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3 Aug, 2022

DHHS adds MPS II to the RUSP for Newborn Screening in the United States

Click here to download full text.Durham, NC August 3, 2022 - The National MPS Society announces that...

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11 Feb, 2022

Advisory Committee on Heritable Disorders in Newborns and Children Votes to Approve MPS II for Recommended Uniform Screening Panel

Download Full Text Durham, NC February 11, 2022 - The National MPS Society announces that the Advisory...

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27 Jul, 2021

Physical Therapy for Children With MPS and ML

Stacey C. Dusing, PT, MSAngela Rosenberg, DrPH, PTSadye Paez, PT, MSWendy Westphal, MPTReviewed and updated...

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