National MPS Society Logo   Donate
MENUMENU
  • Learn
    • Education
      • Newsroom
      • Booklets
      • Fact Sheets
    • Diseases
      • MPS I
      • MPS II
      • MPS III
      • MPS IV
      • MPS VI
      • MPS VII
      • ML II and ML III
    • Treatments
      • ERT
      • HSCT
      • Clinical Trials
      • Emerging Treatments
      • MPS Industry Information
  • Give
    • Fundraising
      • Events
      • Host an Event – FAQ
      • Host a Fundraising Event
      • Host a Run/Walk
      • Volunteer
      • Store
      • Society Sponsored Events
      • 2022 National and Corporate Run/Walk Sponsors
    • Planned Giving
      • Give Today
      • Rising Sun Legacy Circle
      • Bequest a Gift
      • Giving Impact
    • Other
      • Courage Pages
      • Privacy Policy & Donor Rights
      • Matching Gifts
      • Logo Store
  • Support
    • Resources
      • Family Programs
      • Booklets
      • Fact Sheets
      • Physician Database
      • Bereavement
      • Siblings
      • Adult Resource Committee
    • Member Area
      • Newly Diagnosed
      • Pathways Program
      • Become a Member
      • Update Your Membership
      • Login/My Account
    • Remembrance Pages
      • Create/Register a Page
  • Research
    • Society Funded Research Archive
  • Advocacy •
  • Gallery •
  • About
    • Financial Information
      • Audited Financial Reports
      • Unaudited Financial Reports
      • Annual Reports
      • IRS Form 990
    • Board and Bylaws
      • Board and Staff
      • Bylaws
      • Committees
  • Home

ML

Donate Need Support? Fundraising

To evaluate AAV Gene Therapy in the feline model of ML II

The combination of efficacy and safety data on intravenous AAV9 gene therapy from animal models and the preliminary data from human trials are highly encouraging. We therefore believe that intravenous … Continued
December 27, 2017
National MPS Society Logo
  • Learn
  • Give
  • Support
  • Research
  • Advocacy
  • About
MPS Society Four Star Charity Navigator Rated Charity
P.O. Box 14686
Durham, NC 27709-4686
Toll Free: 877.MPS.1001
Local: 919.806.0101

Our Nonprofit 501(c)(3) is: 11-2734849
Copyright © National MPS Society. All Rights Reserved. Web Design & Development by TheeDigital