The National MPS Society exists to cure, support, and advocate for mucopolysaccharidosis (MPS) and mucolipidosis (ML). Thank you for your support and connection with this community. We are honored to … Continued
New Frequently Asked Questions on COVID-19, vaccine distribution, and the impacts on the rare disease community. Click through for some common answers from our CSO and Scientific Advisory Board.
Our December issue of printed Courage is out now, just in time for the holidays! It features 60 full-color pages of stories, family spotlights, program updates, science & research news, fundraising efforts, and more.
Join in on this celebrated day to give. Help us reach our $50,000 goal by making a donation today!
Re-watch the informative conversation with Elsa Shapiro, PhD and Paul Harmatz, MD, on the unique role of the consulting psychologist, building partnerships within the greater trial ecosystem, and considerations for protocol development.
The annual award recognizes exceptional patient leadership advocacy in the field of lysosomal disease. Presentation will take place Monday, February 8, 2021 at the 17th Annual WORLDSymposium.
The recommended framework would qualify many individuals with MPS and ML to be among the first recipients of a COVID-19 vaccine when it becomes available.
National MPS Society Bake Sale and Bake Off starts October 30 - November 7!
Our Virtual Family Conference has concluded but registered attendees can still access it on-demand through October 12th!
Gene Therapy Updates and Pharmacological PresentationsMatthew Ellinwood, DVM, PhDCSO, National MPS Society Dr. Matthew Ellinwood spoke on advances in a subset of gene therapy that involves gene editing. Gene editing … Continued