COVID-19 and MPS/ML: Information and Support

New Frequently Asked Questions on COVID-19, vaccine distribution, and the impacts on the rare disease community. Click through for some common answers from our CSO and Scientific Advisory Board.

Courage Magazine – December 2020

Our December issue of printed Courage is out now, just in time for the holidays! It features 60 full-color pages of stories, family spotlights, program updates, science & research news, fundraising efforts, and more.

Science in MPS and ML

Gene Therapy Updates and Pharmacological PresentationsMatthew Ellinwood, DVM, PhDCSO, National MPS Society Dr. Matthew Ellinwood spoke on advances in a subset of gene therapy that involves gene editing. Gene editing … Continued