Monthly Archives: June 2013

Amicus Therapeutics disclosed a preclinical Chaperone-Advanced Replacement Therapy program for MPS I

Amicus Therapeutics disclosed a preclinical Chaperone-Advanced Replacement Therapy (CHART™) program for MPS I. Amicus is developing a proprietary human recombinant IDUA (rhIDUA) enzyme co-formulated with a novel pharmacological chaperone as …

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Outcome of Janssen advisory panel of MPS experts

Dear MPS Patient advocacy groups; Janssen is pleased to have hosted an advisory panel of MPS experts on May 20th, 2013 and, while we do not have scientific expertise in …

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