Check out our new store items!
40th Anniversary memorabilia & fun new items
Don’t miss the new items in our online store! See our new t-shirt commemorating the National MPS Society’s 40th anniversary. Plus tank tops, shorts, windbreakers, duffel bags, and more!
Give to the 2014 Annual Fund: Chair Lynn Hopkins
Meet Lynn Hopkins, our Chair for the 2014 Annual Fund. Lynn and the National MPS Society hope that your family will make a difference by giving to the 2014 Annual Fund and supporting our mission to keep the Society strong.
28th Annual Family Conference – Disney
The Family Conference in Disney is from December 18-20. Click here for the link to register! Registration deadline – November 26, 2014.
First Treatment for MPS IVA Approved
BioMarin Pharmaceutical announced that the U.S. Food and Drug Administration (FDA) has granted marketing approval for Vimizim™ (elosulfase alfa), the first specific therapy approved for the treatment of Morquio A (MPS IVA syndrome.)
Mucopolysaccharidoses (MPS) and related diseases are genetic lysosomal storage diseases (LSD) caused by the body's inability to produce specific enzymes. Normally, the body uses enzymes to break down and recycle materials in cells. In individuals with MPS and related diseases, the missing or insufficient enzyme prevents the proper recycling process, resulting in the storage of materials in virtually every cell of the body.