February 28th is Rare Disease Day 2015
Rare Disease Day puts the focus on the daily lives of patients, families and caregivers who are living with a rare disease. Show your support!
28th Annual Family Conference – Disney
Thank you to everyone who attended the National MPS Society’s 28th Annual Family Conference December 18-20, 2014 at Disney!
National MPS Society Collaborates to Fund MPS III Gene Therapy
Abeona Therapeutics raises $3.6M to develop therapies for children suffering from MPS III. Gene therapy clinical trials for MPS IIIA and MPS IIIB are anticipated to begin in early to mid-2015.
Have you considered hosting a walk/run?
Have you been thinking about having a Walk/Run in 2015? Hosting an event is a great way to support the National MPS Society. Find out how!
Mucopolysaccharidoses (MPS) and related diseases are genetic lysosomal storage diseases (LSD) caused by the body's inability to produce specific enzymes. Normally, the body uses enzymes to break down and recycle materials in cells. In individuals with MPS and related diseases, the missing or insufficient enzyme prevents the proper recycling process, resulting in the storage of materials in virtually every cell of the body.